Incredibly hard problems, worth every second to solve.

We’re a team driven by an irrepressible passion for science and its ability to transform the world as we know it.

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We Believe:

our bodies have

the answers, we only

need to listen closely.

our bodies have the answers, we only need to listen closely.

scientific integrity

matters more

than notoriety.

scientific integrity matters more than notoriety.

data drives

decision-making.

data drives decision-making.

nothing

is impossible.

nothing is impossible.

everyone deserves

to have a

chance at life.

everyone deserves to have a chance at life.

Together, we’re tackling humanity’s toughest biological challenges through Gene Therapy, impacting lives in ways we can’t express. And, maybe one day, creating a world where ‘incurable’ ceases to be a word.

Geneticists, virologists, molecular biologists, computational biologists and drug development experts

— collectively, we have contributed some of the most cutting-edge technologies and therapies changing the world today.

Adam Dingens, Ph.D.
Scientist
Adrian Briggs, Ph.D.
Senior Director, Head of Technology Development
Anne McGarvey
Research Associate
Anupama Lakshmanan, Ph.D.
Scientist
Ashley Harper
Recruiting Coordinator
Blake Engelbert
Scientist
Brian Booth
Principal Scientist
Chris Nye
Scientist
Clay Patton
Senior Research Associate
Cory Diemler
Senior Research Associate
David Huss, Ph.D.
Vice President, Head of Research
Debojit Bose, Ph.D.
Senior Scientist
Duan Lee
Senior Research Associate
Eric Chadwick
Scientist
Erica Cates
Associate Scientist
Francois Vigneault, Ph.D.
President and CEO
Galina Stepanyuk, Ph.D.
Senior Scientist
Gary Fortin, Ph.D.
Chief Operating Officer (COO)
Grace Campbell
Operations Manager
Heather Brett
Scientist
Henry Lee
Research Associate
Jamie Siemering
HR Manager
Jeffrey Huang, Ph.D.
Senior Scientist
Jeremy Bazinet
Senior Research Associate
John Suliman
CFO & Head of Business Strategy
Karyn Huryn-Selvar
Lab Manager
Katherine Connor, Ph.D.
Director of Operations
Ken Prentice
Director, Head of Process & Product Development
Kevin Stein, Ph.D.
Senior Data Scientist
Lan Guo, Ph.D.
Senior Data Scientist
Lauriel Earley, Ph.D.
Senior Scientist
Liana Stein, Ph.D.
Senior Scientist
Lindsay Deis Huffman, Ph.D.
Senior Scientist
Lisa Taylor Ash
Vice President, Head of Legal
Lucia Shumaker
Research Associate
Marguerite Henderson
Operations Coordinator
Michael Koday
Associate Scientist
Michelle Blake, Ph.D.
Senior Director, Head of Translational Sciences
Paul Meyers
Senior Research Associate
Prashant Mali, Ph.D.
Co-founder and Chair of SAB
Rafael Ponce, Ph.D.
Executive Vice President, Head of Non-Clinical Development
Renuka Ramanathan, Ph.D.
Director of Intellectual Property
Richard Sullivan, Ph.D.
Senior Scientist
Robert Fragoza, Ph.D.
Scientist
Robert Lloyd
Senior Research Associate
Roberto Perales, Ph.D.
Senior Scientist
Ruth Hook
Research Associate
Sandhya Pande, Ph.D.
Senior Scientist
Sandra Shannon
Associate Scientist
Sharon Ke
Senior Research Associate
Stephen Burleigh
Senior Associate Scientist
Susan Byrne, Ph.D.
Principal Scientist
Thomas Long, Ph.D.
Associate Director, Head of Nonclinical Safety
Thomas Packard, Ph.D.
Senior Scientist
Tina Kaur
Senior Accounting Manager
William Johnsen
Senior Associate Scientist
William Krause
Vice President of Finance
Yazmin Rovira Gonzalez, Ph.D.
Scientist
Yiannis Savva, Ph.D.
Senior Scientist
Adam Dingens, Ph.D.
Scientist
Adrian Briggs, Ph.D.
Senior Director, Head of Technology Development
Anne McGarvey
Research Associate
Anupama Lakshmanan, Ph.D.
Scientist
Ashley Harper
Recruiting Coordinator
Blake Engelbert
Scientist
Brian Booth
Principal Scientist
Chris Nye
Scientist
Clay Patton
Senior Research Associate
Cory Diemler
Senior Research Associate
David Huss, Ph.D.
Vice President, Head of Research
Debojit Bose, Ph.D.
Senior Scientist
Duan Lee
Senior Research Associate
Eric Chadwick
Scientist
Erica Cates
Associate Scientist
Francois Vigneault, Ph.D.
President and CEO
Galina Stepanyuk, Ph.D.
Senior Scientist
Gary Fortin, Ph.D.
Chief Operating Officer (COO)
Grace Campbell
Operations Manager
Heather Brett
Scientist
Henry Lee
Research Associate
Jamie Siemering
HR Manager
Jeffrey Huang, Ph.D.
Senior Scientist
Jeremy Bazinet
Senior Research Associate
John Suliman
CFO & Head of Business Strategy
Karyn Huryn-Selvar
Lab Manager
Katherine Connor, Ph.D.
Director of Operations
Ken Prentice
Director, Head of Process & Product Development
Kevin Stein, Ph.D.
Senior Data Scientist
Lan Guo, Ph.D.
Senior Data Scientist
Lauriel Earley, Ph.D.
Senior Scientist
Liana Stein, Ph.D.
Senior Scientist
Lindsay Deis Huffman, Ph.D.
Senior Scientist
Lisa Taylor Ash
Vice President, Head of Legal
Lucia Shumaker
Research Associate
Marguerite Henderson
Operations Coordinator
Michael Koday
Associate Scientist
Michelle Blake, Ph.D.
Senior Director, Head of Translational Sciences
Paul Meyers
Senior Research Associate
Prashant Mali, Ph.D.
Co-founder and Chair of SAB
Rafael Ponce, Ph.D.
Executive Vice President, Head of Non-Clinical Development
Renuka Ramanathan, Ph.D.
Director of Intellectual Property
Richard Sullivan, Ph.D.
Senior Scientist
Robert Fragoza, Ph.D.
Scientist
Robert Lloyd
Senior Research Associate
Roberto Perales, Ph.D.
Senior Scientist
Ruth Hook
Research Associate
Sandhya Pande, Ph.D.
Senior Scientist
Sandra Shannon
Associate Scientist
Sharon Ke
Senior Research Associate
Stephen Burleigh
Senior Associate Scientist
Susan Byrne, Ph.D.
Principal Scientist
Thomas Long, Ph.D.
Associate Director, Head of Nonclinical Safety
Thomas Packard, Ph.D.
Senior Scientist
Tina Kaur
Senior Accounting Manager
William Johnsen
Senior Associate Scientist
William Krause
Vice President of Finance
Yazmin Rovira Gonzalez, Ph.D.
Scientist
Yiannis Savva, Ph.D.
Senior Scientist
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Meet our industry-leading scientific advisory board.
Don Cleveland Ph.D.
Don Cleveland Ph.D. is an award-winning inventor and pioneer in the field of Antisense Oligonucleotide (ASO) and their uses in Gene Therapy. He was recently awarded the Breakthrough Prize in Life Sciences for his work on the pathogenesis of disease and ASO-mediated treatment approaches in ALS and Huntington’s disease. Don is currently Professor of Medicine and Department Chair of Cellular and Molecular Medicine and Neurosciences at the University of California at San Diego, and Head, Laboratory for Cell Biology at the San Diego branch of Ludwig Cancer Research. He has made pioneering discoveries on the mechanisms of chromosome movement and cell-cycle control during normal cellular division, as well as the principles of neuronal cell development and the relationship to defects that contribute to inherited neurodegenerative disease.
George Church, Ph.D.
George Church Ph.D., world-famous geneticist, molecular engineer, and chemist. He developed the methods used for the first genome sequence & million-fold cost reductions since, as well as pioneered many of the CRISPR advances in genome editing. He is currently a Professor of Genetics at Harvard Medical School and Professor of Health Sciences and Technology at Harvard and the Massachusetts Institute of Technology (MIT). He is Director of the U.S. Department of Energy Technology Center and Director of the National Institutes of Health Center of Excellence in Genomic Science. He has received numerous awards, including the 2011 Bower Award and Prize for Achievement in Science from the Franklin Institute and election to the National Academy of Sciences and Engineering.
James Collins, Ph.D.
James Collins Ph.D., is one of the pioneers of the field of synthetic biology and has made multiple synthetic biology and bioengineering breakthroughs in biotechnology and biomedicine. He serves as the Termeer Professor of Medical Engineering & Science and Professor of Biological Engineering at MIT, as well as a member of the Harvard-MIT Health Sciences & Technology Faculty, and core member of the Wyss Institute. His many awards include a Rhodes Scholarship, a MacArthur “Genius Award,” a National Institutes of Health Director’s Pioneer Award. Jim is also an elected member of the National Academy of Sciences, the National Academy of Engineering, the National Academy of Medicine, the American Academy of Arts & Sciences, as well as a charter fellow of the National Academy of Inventors.
Prashant Mali, Ph.D.
Prashant Co-founded ShapeTX and is known for pioneering the development of CRISPR-Cas systems for use in human cells. He is currently Associate Professor in the Department of Bioengineering at the University of California, San Diego where he focuses on developing tools for gene and cell based human therapeutics. Prashant received his Bachelor’s and Master’s in Electrical Engineering from the Indian Institute of Technology Bombay, a doctorate in Biomedical Engineering at the Johns Hopkins University, and a postdoctoral fellowship at Harvard Medical School. He has received numerous awards, including the Siebel Scholar Award, the Burroughs Wellcome Career Award, the Kimmel Scholar Award, to name a few.
Don Cleveland Ph.D.
Don Cleveland Ph.D. is an award-winning inventor and pioneer in the field of Antisense Oligonucleotide (ASO) and their uses in Gene Therapy. He was recently awarded the Breakthrough Prize in Life Sciences for his work on the pathogenesis of disease and ASO-mediated treatment approaches in ALS and Huntington’s disease. Don is currently Professor of Medicine and Department Chair of Cellular and Molecular Medicine and Neurosciences at the University of California at San Diego, and Head, Laboratory for Cell Biology at the San Diego branch of Ludwig Cancer Research. He has made pioneering discoveries on the mechanisms of chromosome movement and cell-cycle control during normal cellular division, as well as the principles of neuronal cell development and the relationship to defects that contribute to inherited neurodegenerative disease.
George Church, Ph.D.
George Church Ph.D., world-famous geneticist, molecular engineer, and chemist. He developed the methods used for the first genome sequence & million-fold cost reductions since, as well as pioneered many of the CRISPR advances in genome editing. He is currently a Professor of Genetics at Harvard Medical School and Professor of Health Sciences and Technology at Harvard and the Massachusetts Institute of Technology (MIT). He is Director of the U.S. Department of Energy Technology Center and Director of the National Institutes of Health Center of Excellence in Genomic Science. He has received numerous awards, including the 2011 Bower Award and Prize for Achievement in Science from the Franklin Institute and election to the National Academy of Sciences and Engineering.
James Collins, Ph.D.
James Collins Ph.D., is one of the pioneers of the field of synthetic biology and has made multiple synthetic biology and bioengineering breakthroughs in biotechnology and biomedicine. He serves as the Termeer Professor of Medical Engineering & Science and Professor of Biological Engineering at MIT, as well as a member of the Harvard-MIT Health Sciences & Technology Faculty, and core member of the Wyss Institute. His many awards include a Rhodes Scholarship, a MacArthur “Genius Award,” a National Institutes of Health Director’s Pioneer Award. Jim is also an elected member of the National Academy of Sciences, the National Academy of Engineering, the National Academy of Medicine, the American Academy of Arts & Sciences, as well as a charter fellow of the National Academy of Inventors.
Prashant Mali, Ph.D.
Prashant Co-founded ShapeTX and is known for pioneering the development of CRISPR-Cas systems for use in human cells. He is currently Associate Professor in the Department of Bioengineering at the University of California, San Diego where he focuses on developing tools for gene and cell based human therapeutics. Prashant received his Bachelor’s and Master’s in Electrical Engineering from the Indian Institute of Technology Bombay, a doctorate in Biomedical Engineering at the Johns Hopkins University, and a postdoctoral fellowship at Harvard Medical School. He has received numerous awards, including the Siebel Scholar Award, the Burroughs Wellcome Career Award, the Kimmel Scholar Award, to name a few.
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Our investors and partners play a pivotal role in advancing Gene Therapy.

Made by great minds, but shaped by steady hearts.

We're continuing to build a team of the brightest in the scientific community. As a culture, we are supported by strong values and a deep belief in honoring science’s purpose to move humanity forward, and let data guide the way.